Following up on previous, dimly received issuances, a new set of ideas published by the FDA to streamline regulatory pathways ...

The MCO-010 vector uses surviving cells in the retina to produce a photosensitive protein that may help patients regain some ...

Treatment introduces an expansion of the scope of gene therapies that might lead to similar treatments for neurodegenerative ...

Cirrus’ lead program is a novel AAV gene therapy designed to restore IRAK-M, a central regulator of the eye’s immune homeostasis, so as to ...

After three patients died, the maker of an investigational gene therapy stopped shipments of the drug after it refused to ...

Stanford researchers and their collaborators have revealed a new device that could change the way scientists conduct ...

Preliminary results from a small trial offer the clearest evidence yet that the brain disease’s progression can be slowed.

Three draft recommendation documents published on Wednesday are intended to guide drug sponsors and accelerate the ...

Cayman Chemical, a global provider of life science research tools, and Akadeum Life Sciences, a leader in buoyancy-based cell ...

How cell and gene therapy developers can lessen the chances of receiving FDA complete response letters through the use of ...

Universities must do more to provide students with cell and gene therapy manufacturing skills, according to a new study.