An international survey of caregivers of individuals with DEEs such as Dravet syndrome (DS) showed major gaps in ...
Patients with transthyretin amyloidosis (ATTR) in China demonstrated high clinical heterogeneity in the recent OverTTuRe ...
A humanized Huntington disease (HD) mouse model showed mild cardiac dysfunction and sex- and brain region-specific metabolic ...
If health care professionals could experience Pompe disease firsthand, they’d learn more than any textbook or lab result ...
The FDA has granted priority review to Roche’s New Drug Application for fenebrutinib in relapsing and primary progressive MS.
The CORE-5 screening tool may be useful for evaluating social risk factors among Black patients with myasthenia gravis (MG).
Two case reports suggest that FSGS may occur secondary to polycythemia vera and that treatment should target the underlying ...
A mother of 2 sons living with FSGS suggests that availability and timing plays a major role in addressing patients' ...
A recent report on nipocalimab presented patient-level postnatal findings through the initial 24 months of life, such as ...
In a new qualitative study, researchers examined how people with Huntington disease (HD) and their carers manage meals.
Patients with indolent SM frequently experience decreased sleep quality that results in subsequent reductions in quality of ...
The FDA has approved an update to the label of sotatercept-csrk to include data from a trial, which tested the drug in newly ...
Some results have been hidden because they may be inaccessible to you
Show inaccessible results