Researchers developed a nanopore sequencing pipeline that may improve genetic diagnosis of repeat expansion disorders, ...
The oral combination of azacitidine and cedazuridine (ASTX030) met its primary endpoint in phase 3 AZTOUND study of patients ...
Older ambulatory patients with DMD who received delandistrogene moxeparvovec in clinical trials maintained more motor ...
A woman with chronic inflammatory demyelinating polyneuropathy (CIDP) shares what it was like to walk in public for the first ...
Allogeneic hematopoietic cell transplantation achieved a 3-year overall survival of 69% in adults aged 18 to 40 years with ...
Shortness of breath seems to be worse in patients with IPF, while cough and quality of life seem worse in patients with PPF.
Shear wave elastography and ultrasound-derived indices exhibit excellent diagnostic performance in detecting interstitial ...
Unclassified generalized epilepsy with myoclonic-tonic seizures may be its own subtype, with different EEG features and ...
The phase 2 LODEFI study results showed 47.4% of patients with MDS achieved the primary endpoint of transfusion independence at 12 months.
Adding rituximab to chemotherapy improved overall survival, progression-free survival, and complete remission rates in newly ...