Patients with GPP carry a higher risk of death and multisystem comorbidities than those with plaque psoriasis, research shows ...
An international survey of caregivers of individuals with DEEs such as Dravet syndrome (DS) showed major gaps in ...
The FDA has granted priority review to Roche’s New Drug Application for fenebrutinib in relapsing and primary progressive MS.
Patients with transthyretin amyloidosis (ATTR) in China demonstrated high clinical heterogeneity in the recent OverTTuRe ...
A humanized Huntington disease (HD) mouse model showed mild cardiac dysfunction and sex- and brain region-specific metabolic ...
A recent report on nipocalimab presented patient-level postnatal findings through the initial 24 months of life, such as ...
If health care professionals could experience Pompe disease firsthand, they’d learn more than any textbook or lab result ...
Two case reports suggest that FSGS may occur secondary to polycythemia vera and that treatment should target the underlying ...
The CORE-5 screening tool may be useful for evaluating social risk factors among Black patients with myasthenia gravis (MG).
A mother of 2 sons living with FSGS suggests that availability and timing plays a major role in addressing patients' ...
The baseline clinical phenotype of older adults with ATTR-CM treated with tafamidis appears to be a stronger predictor of ...
Patients with indolent SM frequently experience decreased sleep quality that results in subsequent reductions in quality of ...